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Abu Dhabi Launches First CRISPR Gene-Editing Therapy for Sickle Cell Disease and Thalassemia
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Abu Dhabi Launches First CRISPR Gene-Editing Therapy for Sickle Cell Disease and Thalassemia

The Department of Health – Abu Dhabi (DoH) has announced the launch of CASGEVY, marking the introduction of the first CRISPR/Cas9 gene-editing therapy in the UAE. This innovative treatment is aimed at patients suffering from sickle cell disease (SCD) and transfusion-dependent beta-thalassemia (TDT) and is provided by the Abu Dhabi Stem Cells Center (ADSCC) in...